巴塞尔大学研发潜在治疗不可治愈肌肉萎缩症的基因疗法
巴塞尔大学的研究人员开发了一种基因疗法，可能用来治疗儿童的一种罕见和目前为止不可治愈的肌肉疾病。研究表明，在动物模型中，单次治疗足以稳定肌肉和神经并停止疾病的进展。现在的挑战是将这一有希望的疗法带入临床试验。
来源: Medical Xpress ｜ 阅读全文
发布时间: 2026-02-27 00:00 GMT+8（北京时间）
#基因疗法 #肌肉萎缩症 #巴塞尔大学
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